Posted on Mon, 09 Jun 2025 13:00:00 +0000
HD starts with a single gene change, but its effects travel many roads. New work shows how brain networks breakdown or reroute. Whether movement, thinking, or mood are most affected, we may be able to guide care in a more personalized direction.
From: HDBuzz
Posted on Wed, 04 Jun 2025 12:23:29 +0000
uniQure has aligned with the US FDA on next steps to achieve accelerated approval of AMT-130. If data remain positive, they will be on track to market the first HD gene therapy.
From: HDBuzz
Posted on Mon, 02 Jun 2025 12:00:00 +0000
Announcing the 2025 HDBuzz Prize for Young Science Writers - sponsored by the Hereditary Disease Foundation!
From: HDBuzz