Posted on Thu, 07 May 2026 13:00:00 +0000
⏱️ 6 min read | While the US regulatory path for AMT-130 remains complicated, uniQure announced plans to seek approval for its HD gene therapy in the UK. Here's what that means, and what might be to come.
From: HDBuzz
Posted on Mon, 04 May 2026 13:00:00 +0000
⏱️10 min read | PTC Therapeutics shared 2-year data for votoplam, a daily HTT-lowering pill. Stage 2 participants showed up to 52% slowing of disease progression. Here's what the data show, what's still missing, and the roll out of the Phase 3 trial.
From: HDBuzz
Posted on Thu, 30 Apr 2026 13:00:00 +0000
⏱️ 8 min read | April 2026 showed us a toxic HTT fragment is center stage in mouse research, CRISPR is showing promise in mouse studies, AI and wearables move closer to the clinic, and 2 studies shine a light on the weight carried by HD caregivers.
From: HDBuzz